This Month In Muscular Dystrophy

Dr. Brian Kaspar Discusses Gene Transfer in Spinal Muscular Atrophy (SMA)

Informações:

Sinopsis

Guest: Brian Kaspar, PhD, Nationwide Children's Hospital Access an abstract of this Month's Featured Research Article: Rescue of the spinal muscular atrophy phenotype in a mouse model by early postnatal delivery of SMN. Nat Biotechnol. 2010 Mar;28(3):271-4.